Duchenne Muscular Dystrophy Awareness Week
Duchenne Muscular Dystrophy Awareness Week, observed from February 13 - 19, is a genetic disorder characterized by progressive muscle degeneration and weakness. It is one of nine types of muscular dystrophy.
Duchenne Muscular Dystrophy is caused by an absence of dystrophin, a protein that helps keep muscle cells intact. Symptom onset is in early childhood, usually between the ages of three and five. The disease primarily affects boys, but in rare cases it can affect girls.
On Sept. 19, 2016, the FDA granted accelerated approval to eteplirsen as the first disease-modifying drug for Duchenne Muscular Dystrophy.